A large genome scan for rare CNVs in amyotrophic lateral sclerosis.

نویسندگان

  • Hylke M Blauw
  • Ammar Al-Chalabi
  • Peter M Andersen
  • Paul W J van Vught
  • Frank P Diekstra
  • Michael A van Es
  • Christiaan G J Saris
  • Ewout J N Groen
  • Wouter van Rheenen
  • Max Koppers
  • Ruben Van't Slot
  • Eric Strengman
  • Karol Estrada
  • Fernando Rivadeneira
  • Albert Hofman
  • Andre G Uitterlinden
  • Lambertus A Kiemeney
  • Sita H M Vermeulen
  • Anna Birve
  • Stefan Waibel
  • Thomas Meyer
  • Simon Cronin
  • Russell L McLaughlin
  • Orla Hardiman
  • Peter C Sapp
  • Martin D Tobin
  • Louise V Wain
  • Barbara Tomik
  • Agnieszka Slowik
  • Robin Lemmens
  • Dan Rujescu
  • Claudia Schulte
  • Thomas Gasser
  • Robert H Brown
  • John E Landers
  • Wim Robberecht
  • Albert C Ludolph
  • Roel A Ophoff
  • Jan H Veldink
  • Leonard H van den Berg
چکیده

Amyotrophic lateral sclerosis (ALS) is a fatal neurodegenerative disease selectively affecting motor neurons in the brain and spinal cord. Recent genome-wide association studies (GWASs) have identified several common variants which increase disease susceptibility. In contrast, rare copy-number variants (CNVs), which have been associated with several neuropsychiatric traits, have not been studied for ALS in well-powered study populations. To examine the role of rare CNVs in ALS susceptibility, we conducted a CNV association study including over 19,000 individuals. In a genome-wide screen of 1875 cases and 8731 controls, we did not find evidence for a difference in global CNV burden between cases and controls. In our association analyses, we identified two loci that met our criteria for follow-up: the DPP6 locus (OR = 3.59, P = 6.6 × 10(-3)), which has already been implicated in ALS pathogenesis, and the 15q11.2 locus, containing NIPA1 (OR = 12.46, P = 9.3 × 10(-5)), the gene causing hereditary spastic paraparesis type 6 (HSP 6). We tested these loci in a replication cohort of 2559 cases and 5887 controls. Again, results were suggestive of association, but did not meet our criteria for independent replication: DPP6 locus: OR = 1.92, P = 0.097, pooled results: OR = 2.64, P = 1.4 × 10(-3); NIPA1: OR = 3.23, P = 0.041, pooled results: OR = 6.20, P = 2.2 × 10(-5)). Our results highlight DPP6 and NIPA1 as candidates for more in-depth studies. Unlike other complex neurological and psychiatric traits, rare CNVs with high effect size do not play a major role in ALS pathogenesis.

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عنوان ژورنال:
  • Human molecular genetics

دوره 19 20  شماره 

صفحات  -

تاریخ انتشار 2010